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Cystic Fibrosis Case Studies

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Cystic Fibrosis Case Studies
Patients with Autoimmune Diseases/ Other Illness
Cystic Fibrosis is a genetic disease that is passed down from both of the parents who have a copy of a defective in their DNA. There are variety of symptoms when it comes to cystic fibrosis such as: ‘Very salty-tasting skin, wheezing or shortness of breath, and male fertility ‘. There are no known cures for this genetic diseases, but there are treatments, and research that can help control this disease, and to possibly make a breakthrough discovery for a cure.
I am patient who suffers from Cystic Fibrosis. I believe that with the stem cell research, it can not only help to understand the disease better and to possibly treat it, but it can help people like me and other who are suffering from the symptoms of this disease. Even though there are no known cures for Cystic Fibrosis, there are certain medications that I can use to help me with my symptoms for example: “Treatments can include antibiotics for frequent lung infections, physiotherapy to help clear the airways of mucus, and drugs to expand the airways. In some cases, a lung transplant may also be necessary “(Cystic Fibrosis and stem cells 1).
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The study suggest that umbilical cord blood could be used to restore lung function…’The Cystic Fibrosis Trust’ has also funded a project to correct two rare mutations of the Cystic Fibrosis gene. The project will use induced pluripotent stem cells made from white blood cells along with gene repair and editing technology to repair the two rare ‘stop condon’ mutations “(Cystic Fibrosis

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